The European Commission has approved the world's first gene therapy for children suffering from ADA-SCID, a rare disorder closely linked to the "bubble boy" disease. The new treatment uses gene-editing techniques to fix the faulty gene.
The European Commission has approved the world's first gene therapy for children suffering from ADA-SCID, a rare disorder closely linked to the "bubble boy" disease. The new treatment uses gene-editing techniques to fix the faulty gene.